Browsing by Author Zabaleta-Lasarte, N. (Nerea)

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Showing results 1 to 6 of 6
Issue DateTitleTypeAuthor(s)
22-Feb-2024Advances in precision and safety of CRISPR-based gene targeting for Primary Hyperoxaluria Type 1TesisTorella, L. (Laura)
2018CRISPR/Cas9-mediated glycolate oxidase disruption is an efficacious and safe treatment for primary hyperoxaluria type IArticuloZabaleta-Lasarte, N. (Nerea); Barberia, M. (Miren); Martin-Higueras, C. (Cristina); Zapata-Linares, N.M. (Natalia María); Betancor, I. (Isabel); Rodriguez, S. (Saray); Martínez-Turrillas, R. (Rebeca); Torella, L. (Laura); Vales, A. (África); Olagüe, M. (María); Vilas, A. (Amaia); Castro-Labrador, L. (Laura); Lara-Astiaso, D. (David); Prosper-Cardoso, F. (Felipe); Salido, E. (Eduardo); González-Aseguinolaza, G. (Gloria); Rodriguez-Madoz, J.R. (Juan Roberto)
30-Oct-2018Development of the advanced genetic therapies for Primary Hyperoxaluria type ITesisZabaleta-Lasarte, N. (Nerea)
2020In Vitro and In Vivo Genetic Disease Modeling via NHEJ-Precise Deletions Using CRISPR-Cas9ArticuloLópez-Manzaneda, S. (Sergio); Ojeda-Pérez, I. (Isabel); Zabaleta-Lasarte, N. (Nerea); García-Torralba, A. (Aída); Alberquilla, O. (Omaira); Torres, R. (Raúl); Sánchez-Domínguez, R. (Rebeca); Torella, L. (Laura); Olivier, E. (Emmanuel); Mountford, J. (Joanne); Ramírez, J.C. (Juan C.); Bueren, J.A. (Juan A.); González-Aseguinolaza, G. (Gloria); Segovia, J.C. (Jose-Carlos)
2020Inhibition of MicroRNA 6937 Delays Photoreceptor and Vision Loss in a Mouse Model of Retinitis PigmentosaArticuloAnasagasti, A. (Ander); López, A. (Andrés); Milla-Navarro, S. (Santiago); Escudero-Arrarás, L. (Leire); Rodríguez-Hidalgo, M. (María); Zabaleta-Lasarte, N. (Nerea); González-Aseguinolaza, G. (Gloria); de-la-Villa, P. (Pedro); Ruiz-Ederra, J. (Javier)
2022mRNA and gene editing: Late breaking therapies in liver diseasesArticuloZabaleta-Lasarte, N. (Nerea); Torella, L. (Laura); Weber, N.D. (Nicholas D.); González-Aseguinolaza, G. (Gloria)